⏰ when
When was gene therapy first used successfully in a human patient?
Quick Answer
A landmark successful gene therapy trial took place in 1990. It treated a child with severe combined immunodeficiency.
The Full Story
In 1990, researchers treated a four-year-old girl, Ashanti DeSilva, with gene therapy for adenosine deaminase deficiency, a form of severe combined immunodeficiency. The treatment was the first widely recognized successful use of gene therapy in a human patient. It did not cure all cases of the disorder, but it proved that genetic treatment in humans was possible. The event opened a new era in medical genetics.
Key Facts
1.First major human gene therapy in 1990
2.Patient was Ashanti DeSilva
3.Target disorder was ADA-SCID
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Suggested video title for this topic:
"The first real gene therapy success"
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